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Eteplirsen

Authors: 
The LiverTox team
Citation: 
LiverTox: Clinical and Research Information on Drug-Induced Liver Injury [Internet]. Bethesda (MD): National Institute of Diabetes and Digestive and Kidney Diseases; 2012-. 2020 Feb 27
Abstract: 
Eteplirsen is synthetic antisense oligonucleotide designed to cause skipping of abnormal exons during synthesis of the dystrophin gene and that is used to treat Duchenne muscular dystrophy. Clinical experience with eteplirsen has been limited, but it has not been linked to serum enzyme elevations or to instances of acute liver injury with symptoms and jaundice.
Epub: 
Not Epub