Shift Pharmaceuticals Orphan Drug: Morpholino for Spinal Muscular Atrophy

Shift Pharmaceuticals receives an Orphan Drug designation from the FDA for their Morpholino to treat Spinal Muscular Atrophy.

https://smauk.org.uk/blog/treatments-research/shift-pharmaceuticals-rece...

https://www.accessdata.fda.gov/scripts/opdlisting/oopd/detailedIndex.cfm...